SMPD1 Chromosome 11

Sphingomyelin phosphodiesterase 1
406 variants 406 Health Risk

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What This Gene Does
The protein encoded by this gene is a lysosomal acid sphingomyelinase that converts sphingomyelin to ceramide. The encoded protein also has phospholipase C activity. Defects in this gene are a cause of Niemann-Pick disease type A (NPA) and Niemann-Pick disease type B (NPB). Multiple transcript variants encoding different isoforms have been identified. [provided by RefSeq, Jul 2010]
Associated Conditions (19)
Niemann-Pick disease
type A
type B
Sphingomyelin/cholesterol lipidosis
Inborn genetic diseases
SMPD1-related disorder
Gaucher disease
Intellectual disability
Lysosomal storage disease
Abnormality of metabolism/homeostasis
Niemann-pick disease
intermediate
protracted neurovisceral
Acid sphingomyelinase deficiency
See cases
type C1
Ceroid lipofuscinosis
neuronal
6A
Key Variants
All Variants (406)
RSID Category Clinical Significance Conditions
RS875989835 Health Risk Pathogenic Niemann-Pick disease, type A, Niemann-Pick disease
RS875989837 Health Risk Pathogenic Niemann-Pick disease, type A, Niemann-Pick disease
RS886043098 Health Risk Pathogenic Niemann-Pick disease, type A, Niemann-Pick disease
RS943865463 Health Risk Pathogenic Niemann-Pick disease, type A, Niemann-Pick disease
RS1057516432 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS1057516454 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, Sphingomyelin/cholesterol lipidosis
RS1057517195 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS120074119 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, Sphingomyelin/cholesterol lipidosis
RS120074121 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, Sphingomyelin/cholesterol lipidosis
RS120074124 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, Sphingomyelin/cholesterol lipidosis
RS1205990349 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS1319643225 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS1342372980 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS1470998208 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS1554933746 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS1554934212 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS1554935136 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS1554935669 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS1564923612 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS1590739350 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, Sphingomyelin/cholesterol lipidosis
RS1590743683 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS1847910654 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS1847955457 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS199915216 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS201550531 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS2134004594 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS2134006149 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS2134006179 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS2134021058 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS2493805239 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS2493805504 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS2493813438 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS2493813577 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS2493822055 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS267607074 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS281860676 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type B, type A
RS398123479 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS727504165 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS727504166 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS747143343 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS750779804 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS751269562 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS752000778 Health Risk Pathogenic/Likely pathogenic Intellectual disability, Sphingomyelin/cholesterol lipidosis, Niemann-Pick disease
RS756366019 Health Risk Pathogenic/Likely pathogenic Sphingomyelin/cholesterol lipidosis, Niemann-Pick disease, type A
RS759389193 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS764317969 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS767492080 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS771336819 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, Niemann-Pick disease
RS776442314 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
RS780134410 Health Risk Pathogenic/Likely pathogenic Niemann-Pick disease, type A, type B
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