PUS1 Chromosome 12

Pseudouridine synthase 1
79 variants 79 Health Risk

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What This Gene Does
This gene encodes a pseudouridine synthase that converts uridine to pseudouridine once it has been incorporated into an RNA molecule. The encoded enzyme may play an essential role in tRNA function and in stabilizing the secondary and tertiary structure of many RNAs. A mutation in this gene has been linked to mitochondrial myopathy and sideroblastic anemia. Alternate splicing results in multiple transcript variants.[provided by RefSeq, Sep 2009]
Gene Info
Gene Group
Pseudouridine synthases
Locus Type
gene with protein product
Location
12q24.33
Ensembl
ENSG00000177192
Associated Conditions (7)
Myopathy
lactic acidosis
and sideroblastic anemia 1
PUS1-related disorder
Inborn genetic diseases
and sideroblastic anemia
Sulfite oxidase deficiency due to molybdenum cofactor deficiency type B
Key Variants
All Variants (79)
RSID Category Clinical Significance Conditions
RS1045133170 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS138198591 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS143660941 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS145430883 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS148057665 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS149324363 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS199863621 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS200065515 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS200591614 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS201441662 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS201541270 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS201753270 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS371752870 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS372753711 Health Risk Conflicting classifications of pathogenicity
RS554459931 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS755540245 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS760191922 Health Risk Conflicting classifications of pathogenicity
RS761064906 Health Risk Conflicting classifications of pathogenicity
RS761410867 Health Risk Conflicting classifications of pathogenicity PUS1-related disorder, PUS1-related disorder
RS761456442 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS766451588 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS771486572 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS863224174 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS863224176 Health Risk Conflicting classifications of pathogenicity
RS886049093 Health Risk Conflicting classifications of pathogenicity Myopathy, lactic acidosis, and sideroblastic anemia 1
RS1399740294 Health Risk Likely pathogenic
RS1450284892 Health Risk Likely pathogenic
RS2136428856 Health Risk Likely pathogenic
RS2136432221 Health Risk Likely pathogenic
RS2540870135 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS2540870199 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS2540870303 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS2540872758 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS2540873492 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS2540873523 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS2540873585 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS2540874019 Health Risk Likely pathogenic PUS1-related disorder, Myopathy, lactic acidosis
RS2541388135 Health Risk Likely pathogenic PUS1-related disorder, Myopathy, lactic acidosis
RS2541388364 Health Risk Likely pathogenic
RS2541388990 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS2541389252 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS751632633 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS869025309 Health Risk Likely pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS1048018914 Health Risk Pathogenic Myopathy, lactic acidosis, and sideroblastic anemia
RS104894372 Health Risk Pathogenic Myopathy, lactic acidosis, and sideroblastic anemia 1
RS1207533798 Health Risk Pathogenic
RS1890524790 Health Risk Pathogenic
RS1891062680 Health Risk Pathogenic
RS1891068271 Health Risk Pathogenic
RS1891080553 Health Risk Pathogenic
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