NPHP4 Chromosome 1

Nephrocystin 4
274 variants 274 Health Risk

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What This Gene Does
This gene encodes a protein involved in renal tubular development and function. This protein interacts with nephrocystin, and belongs to a multifunctional complex that is localized to actin- and microtubule-based structures. Mutations in this gene are associated with nephronophthisis type 4, a renal disease, and with Senior-Loken syndrome type 4, a combination of nephronophthisis and retinitis pigmentosa. Alternative splicing results in multiple transcript variants. [provided by RefSeq, Apr 2014]
Gene Info
Gene Group
NPHP complex
Locus Type
gene with protein product
Location
1p36.31
Ensembl
ENSG00000131697
Associated Conditions (32)
Nephronophthisis
NPHP4-related disorder
Nephronophthisis 4
Senior-Loken syndrome 4
Inborn genetic diseases
Focal segmental glomerulosclerosis
Kidney disorder
Malignant tumor of esophagus
Familial cancer of breast
Acute myeloid leukemia
Cervical cancer
Sarcoma
Thyroid cancer
nonmedullary
1
Melanoma
Retinal dystrophy
Cholestasis
Congenital anomaly of kidney and urinary tract
Atypical hemolytic-uremic syndrome
+12 more conditions
Key Variants
All Variants (274)
RSID Category Clinical Significance Conditions
RS775221217 Health Risk Pathogenic Nephronophthisis, Senior-Loken syndrome 4, Nephronophthisis
RS775612958 Health Risk Pathogenic Nephronophthisis 4, Nephronophthisis, Nephronophthisis 4
RS776535691 Health Risk Pathogenic Nephronophthisis, Nephronophthisis 4, Senior-Loken syndrome 4
RS777884325 Health Risk Pathogenic Nephronophthisis, Nephronophthisis
RS780268322 Health Risk Pathogenic Nephronophthisis, Nephronophthisis
RS997408852 Health Risk Pathogenic Nephronophthisis, Nephronophthisis 4, Nephronophthisis
RS1168286961 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Nephronophthisis 4, Senior-Loken syndrome 4
RS1179512510 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Senior-Loken syndrome 4, Nephronophthisis 4
RS1210874691 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Nephronophthisis 4, Senior-Loken syndrome 4
RS1235304713 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Nephronophthisis 4, Senior-Loken syndrome 4
RS1368105372 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Nephronophthisis 4, Senior-Loken syndrome 4
RS1414888414 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Senior-Loken syndrome 4, Nephronophthisis 4
RS1474013513 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Nephronophthisis 4, Senior-Loken syndrome 4
RS1553178047 Health Risk Pathogenic/Likely pathogenic Nephronophthisis 4, Senior-Loken syndrome 4, Nephronophthisis
RS1553200990 Health Risk Pathogenic/Likely pathogenic Nephronophthisis 4, Nephronophthisis, Nephronophthisis 4
RS2100466824 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Nephronophthisis 4, Nephronophthisis
RS2100620614 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Senior-Loken syndrome 4, Nephronophthisis 4
RS370210428 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Senior-Loken syndrome 4, NPHP4-related disorder
RS751662952 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Nephronophthisis 4, Senior-Loken syndrome 4
RS756111113 Health Risk Pathogenic/Likely pathogenic Retinal dystrophy, Kidney disorder, Senior-Loken syndrome 4
RS758275952 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Nephronophthisis 4, Senior-Loken syndrome 4
RS762371581 Health Risk Pathogenic/Likely pathogenic Nephronophthisis 4, Senior-Loken syndrome 4, Nephronophthisis 4
RS780905861 Health Risk Pathogenic/Likely pathogenic Senior-Loken syndrome 4, Kidney disorder, Nephronophthisis
RS781558715 Health Risk Pathogenic/Likely pathogenic Nephronophthisis, Nephronophthisis 4, Senior-Loken syndrome 4
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