MYSM1 Chromosome 1

Myb like, SWIRM and MPN domains 1
33 variants 33 Health Risk

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What This Gene Does
Enables deubiquitinase activity; histone binding activity; and transcription coactivator activity. Involved in chromatin remodeling; positive regulation of transcription by RNA polymerase II; and regulation of hemopoiesis. Located in nucleolus and nucleoplasm. Part of protein-containing complex. Implicated in diabetic retinopathy. [provided by Alliance of Genome Resources, Jul 2025]
Gene Info
Gene Group
"Myb/SANT domain containing|JAMM/MPN+ metallopeptidase family"
Locus Type
gene with protein product
Location
1p32.1
Ensembl
ENSG00000162601
Associated Conditions (4)
MYSM1-related disorder
Inborn genetic diseases
Bone marrow failure syndrome 4
Clear cell carcinoma of kidney
Key Variants
All Variants (33)
RSID Category Clinical Significance Conditions
RS186559420 Health Risk Conflicting classifications of pathogenicity MYSM1-related disorder, Inborn genetic diseases, MYSM1-related disorder
RS199949280 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS202033823 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS371957963 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS551018622 Health Risk Conflicting classifications of pathogenicity
RS569512271 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, MYSM1-related disorder, Inborn genetic diseases
RS758032156 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS767560916 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS770840414 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS1307057213 Health Risk Likely pathogenic
RS1569692271 Health Risk Likely pathogenic
RS201886018 Health Risk Likely pathogenic Bone marrow failure syndrome 4, MYSM1-related disorder, Clear cell carcinoma of kidney
RS2524280386 Health Risk Likely pathogenic Bone marrow failure syndrome 4, Bone marrow failure syndrome 4
RS558614618 Health Risk Likely pathogenic
RS1038285646 Health Risk Pathogenic
RS1175570663 Health Risk Pathogenic
RS1557507208 Health Risk Pathogenic Bone marrow failure syndrome 4, Bone marrow failure syndrome 4
RS1557518298 Health Risk Pathogenic Bone marrow failure syndrome 4, Bone marrow failure syndrome 4
RS1569770360 Health Risk Pathogenic Bone marrow failure syndrome 4, Bone marrow failure syndrome 4
RS1644486654 Health Risk Pathogenic Bone marrow failure syndrome 4, Bone marrow failure syndrome 4
RS2100658801 Health Risk Pathogenic
RS2100658808 Health Risk Pathogenic
RS2524279750 Health Risk Pathogenic
RS2524284551 Health Risk Pathogenic
RS2524285749 Health Risk Pathogenic
RS2524330840 Health Risk Pathogenic
RS2524357635 Health Risk Pathogenic
RS536775508 Health Risk Pathogenic
RS748065332 Health Risk Pathogenic
RS755178846 Health Risk Pathogenic
RS775930259 Health Risk Pathogenic
RS780757165 Health Risk Pathogenic Bone marrow failure syndrome 4, Bone marrow failure syndrome 4
RS866468317 Health Risk Pathogenic Bone marrow failure syndrome 4, Bone marrow failure syndrome 4
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