UBA1 Chromosome X

Ubiquitin like modifier activating enzyme 1
27 variants 27 Health Risk

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What This Gene Does
The protein encoded by this gene catalyzes the first step in ubiquitin conjugation to mark cellular proteins for degradation. This gene complements an X-linked mouse temperature-sensitive defect in DNA synthesis, and thus may function in DNA repair. It is part of a gene cluster on chromosome Xp11.23. Alternatively spliced transcript variants that encode the same protein have been described. [provided by RefSeq, Jul 2008]
Gene Info
Gene Group
"Ubiquitin like modifier activating enzymes|Cilia and flagella associated"
Locus Type
gene with protein product
Location
Xp11.3
Ensembl
ENSG00000130985
Associated Conditions (7)
Infantile-onset X-linked spinal muscular atrophy
Inborn genetic diseases
VEXAS syndrome
VEXAS
UBA1-related disorder
Congenital portosystemic shunt
Nonpapillary renal cell carcinoma
Key Variants
RS1173482035
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
Health Risk
RS140950898
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
Health Risk
RS148642741
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
Health Risk
RS1556787651
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, VEXAS syndrome, Inborn genetic diseases
Health Risk
RS1556788826
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
Health Risk
RS185589110
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
Health Risk
RS1936307795
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, VEXAS syndrome, VEXAS
Health Risk
RS200541240
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
Health Risk
RS368506746
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, Infantile-onset X-linked spinal muscular atrophy
Health Risk
RS370565575
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
Health Risk
RS373305404
Conflicting classifications of pathogenicity
Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Congenital portosystemic shunt
Health Risk
RS377527446
Conflicting classifications of pathogenicity
Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases
Health Risk
All Variants (27)
RSID Category Clinical Significance Conditions
RS1173482035 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS140950898 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS148642741 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS1556787651 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, VEXAS syndrome, Inborn genetic diseases
RS1556788826 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS185589110 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS1936307795 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, VEXAS syndrome, VEXAS
RS200541240 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS368506746 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Infantile-onset X-linked spinal muscular atrophy
RS370565575 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS373305404 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Congenital portosystemic shunt
RS377527446 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases
RS5906354 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS781838601 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS781873529 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Infantile-onset X-linked spinal muscular atrophy
RS781909775 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS782097752 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS782416867 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, VEXAS, VEXAS syndrome
RS782451807 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS782527493 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS782712220 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Infantile-onset X-linked spinal muscular atrophy
RS782727078 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS782781187 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Infantile-onset X-linked spinal muscular atrophy
RS782796398 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS80356547 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS888369922 Health Risk Conflicting classifications of pathogenicity Infantile-onset X-linked spinal muscular atrophy, Inborn genetic diseases, Infantile-onset X-linked spinal muscular atrophy
RS2147273055 Health Risk Likely pathogenic
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