PSAP Chromosome 10

Prosaposin
117 variants 117 Health Risk

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What This Gene Does
This gene encodes a highly conserved preproprotein that is proteolytically processed to generate four main cleavage products including saposins A, B, C, and D. Each domain of the precursor protein is approximately 80 amino acid residues long with nearly identical placement of cysteine residues and glycosylation sites. Saposins A-D localize primarily to the lysosomal compartment where they facilitate the catabolism of glycosphingolipids with short oligosaccharide groups. The precursor protein exists both as a secretory protein and as an integral membrane protein and has neurotrophic activities. Mutations in this gene have been associated with Gaucher disease and metachromatic leukodystrophy. Alternative splicing results in multiple transcript variants, at least one of which encodes an isoform that is proteolytically processed. [provided by RefSeq, Feb 2016]
Gene Info
Gene Group
Receptor ligands
Locus Type
gene with protein product
Location
10q22.1
Ensembl
ENSG00000197746
Associated Conditions (13)
Gaucher disease due to saposin C deficiency
Krabbe disease due to saposin A deficiency
Combined PSAP deficiency
Sphingolipid activator protein 1 deficiency
Metachromatic leukodystrophy
PSAP-related disorder
Inborn genetic diseases
Neuromuscular disease
Parkinson disease 24
autosomal dominant
susceptibility to
Melanoma
Hepatocellular carcinoma
Key Variants
RS111369573
Conflicting classifications of pathogenicity
Gaucher disease due to saposin C deficiency, Krabbe disease due to saposin A deficiency, Combined PSAP deficiency
Health Risk
RS113284884
Conflicting classifications of pathogenicity
Combined PSAP deficiency, Sphingolipid activator protein 1 deficiency, Gaucher disease due to saposin C deficiency
Health Risk
RS138010978
Conflicting classifications of pathogenicity
Sphingolipid activator protein 1 deficiency, Krabbe disease due to saposin A deficiency, Gaucher disease due to saposin C deficiency
Health Risk
RS138328594
Conflicting classifications of pathogenicity
Sphingolipid activator protein 1 deficiency, Krabbe disease due to saposin A deficiency, Gaucher disease due to saposin C deficiency
Health Risk
RS138880818
Conflicting classifications of pathogenicity
Combined PSAP deficiency, Sphingolipid activator protein 1 deficiency, Krabbe disease due to saposin A deficiency
Health Risk
RS139178900
Conflicting classifications of pathogenicity
Krabbe disease due to saposin A deficiency, Combined PSAP deficiency, Gaucher disease due to saposin C deficiency
Health Risk
RS140066253
Conflicting classifications of pathogenicity
Gaucher disease due to saposin C deficiency, Combined PSAP deficiency, Sphingolipid activator protein 1 deficiency
Health Risk
RS141133813
Conflicting classifications of pathogenicity
Gaucher disease due to saposin C deficiency, Combined PSAP deficiency, Krabbe disease due to saposin A deficiency
Health Risk
RS141199649
Conflicting classifications of pathogenicity
Gaucher disease due to saposin C deficiency, Krabbe disease due to saposin A deficiency, Combined PSAP deficiency
Health Risk
RS141906397
Conflicting classifications of pathogenicity
Combined PSAP deficiency, Krabbe disease due to saposin A deficiency, Sphingolipid activator protein 1 deficiency
Health Risk
RS144942998
Conflicting classifications of pathogenicity
Combined PSAP deficiency, Krabbe disease due to saposin A deficiency, Gaucher disease due to saposin C deficiency
Health Risk
RS147046509
Conflicting classifications of pathogenicity
Combined PSAP deficiency, Sphingolipid activator protein 1 deficiency, Krabbe disease due to saposin A deficiency
Health Risk
All Variants (117)
RSID Category Clinical Significance Conditions
RS1554879741 Health Risk Likely pathogenic Combined PSAP deficiency, Krabbe disease due to saposin A deficiency, Sphingolipid activator protein 1 deficiency
RS1554879785 Health Risk Likely pathogenic
RS1554881272 Health Risk Likely pathogenic Inborn genetic diseases, Krabbe disease due to saposin A deficiency, PSAP-related disorder
RS1589446748 Health Risk Likely pathogenic Combined PSAP deficiency, Sphingolipid activator protein 1 deficiency, Combined PSAP deficiency
RS1842392331 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Krabbe disease due to saposin A deficiency, Sphingolipid activator protein 1 deficiency
RS2133029725 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2133030537 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2133043288 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2133047947 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Melanoma, Sphingolipid activator protein 1 deficiency
RS2133053107 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494497146 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494522736 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494523338 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494532805 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494533554 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS759960679 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Metachromatic leukodystrophy, Sphingolipid activator protein 1 deficiency
RS760391023 Health Risk Likely pathogenic Combined PSAP deficiency, Combined PSAP deficiency
RS772826932 Health Risk Likely pathogenic Combined PSAP deficiency, Combined PSAP deficiency
RS779384030 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Hepatocellular carcinoma, Sphingolipid activator protein 1 deficiency
RS949729827 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS971589777 Health Risk Likely pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS121918105 Health Risk Pathogenic Gaucher disease due to saposin C deficiency, Gaucher disease due to saposin C deficiency
RS121918106 Health Risk Pathogenic Combined PSAP deficiency, Gaucher disease due to saposin C deficiency, Sphingolipid activator protein 1 deficiency
RS121918108 Health Risk Pathogenic Gaucher disease due to saposin C deficiency, Gaucher disease due to saposin C deficiency
RS121918109 Health Risk Pathogenic Gaucher disease due to saposin C deficiency, Gaucher disease due to saposin C deficiency
RS1244889985 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS1436008939 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS1489308019 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS1554880848 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Metachromatic leukodystrophy, Sphingolipid activator protein 1 deficiency
RS1564815053 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS1589451049 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Parkinson disease 24, autosomal dominant
RS1589451050 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS1842248191 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS1842310280 Health Risk Pathogenic Combined PSAP deficiency, Combined PSAP deficiency
RS1842351095 Health Risk Pathogenic
RS1842392268 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2133031097 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2133031639 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2133043442 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2133048124 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2133049150 Health Risk Pathogenic Krabbe disease due to saposin A deficiency, Krabbe disease due to saposin A deficiency
RS2133053013 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494494292 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494498245 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494498363 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494506149 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494516860 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494516881 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494525612 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
RS2494525720 Health Risk Pathogenic Sphingolipid activator protein 1 deficiency, Sphingolipid activator protein 1 deficiency
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