PNPLA1 Chromosome 6

Patatin like domain 1, omega-hydroxyceramide transacylase
55 variants 55 Health Risk

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What This Gene Does
The protein encoded by this gene belongs to the patatin-like phospholipase (PNPLA) family, which is characterized by the presence of a highly conserved patatin domain. PNPLA family members have diverse lipolytic and acyltransferase activities, and are key elements in lipid metabolism. While other members of this family have been well characterized, the function of this gene remained an enigma. However, recent studies show that this gene is expressed in the skin epidermal keratinocytes, and has a role in glycerophospholipid metabolism in the cutaneous barrier. Consistent with these observations, mutations in this gene are associated with ichthyosis in human (autosomal recessive congenital ichthyoses, ARCI) and dog. Alternatively spliced transcript variants encoding different isoforms have been found for this gene. [provided by RefSeq, Jun 2012]
Gene Info
Gene Group
Patatin like phospholipase domain containing
Locus Type
gene with protein product
Location
6p21.31
Ensembl
ENSG00000180316
Associated Conditions (8)
Autosomal recessive congenital ichthyosis 10
Inborn genetic diseases
PNPLA1-related disorder
Lamellar ichthyosis
Congenital ichthyosiform erythroderma
Abnormality of the skin
Ichthyosis
Autosomal recessive congenital ichthyosis
Key Variants
RS1029691431
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, Inborn genetic diseases, Autosomal recessive congenital ichthyosis 10
Health Risk
RS139173161
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
Health Risk
RS139909055
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, Inborn genetic diseases, Autosomal recessive congenital ichthyosis 10
Health Risk
RS140585347
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, PNPLA1-related disorder, Autosomal recessive congenital ichthyosis 10
Health Risk
RS141744967
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
Health Risk
RS148471904
Conflicting classifications of pathogenicity
Inborn genetic diseases, Inborn genetic diseases
Health Risk
RS1561853887
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, Lamellar ichthyosis, Autosomal recessive congenital ichthyosis 10
Health Risk
RS185312959
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, PNPLA1-related disorder, Autosomal recessive congenital ichthyosis 10
Health Risk
RS201125928
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
Health Risk
RS201231660
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
Health Risk
RS2533200721
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
Health Risk
RS371283191
Conflicting classifications of pathogenicity
Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
Health Risk
All Variants (55)
RSID Category Clinical Significance Conditions
RS1029691431 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Inborn genetic diseases, Autosomal recessive congenital ichthyosis 10
RS139173161 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS139909055 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Inborn genetic diseases, Autosomal recessive congenital ichthyosis 10
RS140585347 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, PNPLA1-related disorder, Autosomal recessive congenital ichthyosis 10
RS141744967 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS148471904 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS1561853887 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Lamellar ichthyosis, Autosomal recessive congenital ichthyosis 10
RS185312959 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, PNPLA1-related disorder, Autosomal recessive congenital ichthyosis 10
RS201125928 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS201231660 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS2533200721 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS371283191 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS372072356 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, PNPLA1-related disorder, Autosomal recessive congenital ichthyosis 10
RS373131816 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS373711651 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS375901638 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS376245108 Health Risk Conflicting classifications of pathogenicity Congenital ichthyosiform erythroderma, Congenital ichthyosiform erythroderma
RS561297650 Health Risk Conflicting classifications of pathogenicity Inborn genetic diseases, Inborn genetic diseases
RS748310345 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS749816424 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS761075511 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS766215523 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS767322248 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS770164167 Health Risk Conflicting classifications of pathogenicity Autosomal recessive congenital ichthyosis 10, PNPLA1-related disorder, Autosomal recessive congenital ichthyosis 10
RS1170446813 Health Risk Likely pathogenic Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS1373230987 Health Risk Likely pathogenic Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS2127346823 Health Risk Likely pathogenic Abnormality of the skin, Abnormality of the skin
RS746575171 Health Risk Likely pathogenic Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS766188849 Health Risk Likely pathogenic Congenital ichthyosiform erythroderma, Lamellar ichthyosis, Autosomal recessive congenital ichthyosis 10
RS767462752 Health Risk Likely pathogenic
RS777268917 Health Risk Likely pathogenic Lamellar ichthyosis, Autosomal recessive congenital ichthyosis 10, Lamellar ichthyosis
RS922934422 Health Risk Likely pathogenic Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS938583000 Health Risk Likely pathogenic Lamellar ichthyosis, Lamellar ichthyosis
RS1231123861 Health Risk Pathogenic Congenital ichthyosiform erythroderma, Congenital ichthyosiform erythroderma
RS1407871103 Health Risk Pathogenic Congenital ichthyosiform erythroderma, Congenital ichthyosiform erythroderma
RS1554139129 Health Risk Pathogenic
RS1561853847 Health Risk Pathogenic Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS1561864453 Health Risk Pathogenic Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS1582046125 Health Risk Pathogenic Congenital ichthyosiform erythroderma, Lamellar ichthyosis, Congenital ichthyosiform erythroderma
RS1582078740 Health Risk Pathogenic Congenital ichthyosiform erythroderma, Autosomal recessive congenital ichthyosis 10, Congenital ichthyosiform erythroderma
RS1582081682 Health Risk Pathogenic Congenital ichthyosiform erythroderma, Congenital ichthyosiform erythroderma
RS1582086407 Health Risk Pathogenic Autosomal recessive congenital ichthyosis 10, Autosomal recessive congenital ichthyosis 10
RS2533200460 Health Risk Pathogenic
RS373148099 Health Risk Pathogenic Congenital ichthyosiform erythroderma, Lamellar ichthyosis, Congenital ichthyosiform erythroderma
RS748240234 Health Risk Pathogenic
RS753687060 Health Risk Pathogenic Congenital ichthyosiform erythroderma, Autosomal recessive congenital ichthyosis 10, Congenital ichthyosiform erythroderma
RS778158406 Health Risk Pathogenic
RS1182312612 Health Risk Pathogenic/Likely pathogenic Autosomal recessive congenital ichthyosis 10, Congenital ichthyosiform erythroderma, Autosomal recessive congenital ichthyosis 10
RS1207879599 Health Risk Pathogenic/Likely pathogenic Congenital ichthyosiform erythroderma, Autosomal recessive congenital ichthyosis 10, Congenital ichthyosiform erythroderma
RS1554138062 Health Risk Pathogenic/Likely pathogenic Autosomal recessive congenital ichthyosis 10, Congenital ichthyosiform erythroderma, Lamellar ichthyosis
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