PCSK9 Chromosome 1

Proprotein convertase subtilisin/kexin type 9
167 variants 167 Health Risk

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What This Gene Does
This gene encodes a member of the subtilisin-like proprotein convertase family, which includes proteases that process protein and peptide precursors trafficking through regulated or constitutive branches of the secretory pathway. The encoded protein undergoes an autocatalytic processing event with its prosegment in the ER and is constitutively secreted as an inactive protease into the extracellular matrix and trans-Golgi network. It is expressed in liver, intestine and kidney tissues and escorts specific receptors for lysosomal degradation. It plays a role in cholesterol and fatty acid metabolism. Mutations in this gene have been associated with autosomal dominant familial hypercholesterolemia. Alternative splicing results in multiple transcript variants. [provided by RefSeq, Feb 2014]
Gene Info
Gene Group
Proprotein convertase subtilisin/kexin family
Locus Type
gene with protein product
Location
1p32.3
Ensembl
ENSG00000169174
Associated Conditions (16)
Familial hypercholesterolemia
Hypercholesterolemia
autosomal dominant
3
Hypobetalipoproteinemia
familial
1
Cardiovascular phenotype
PCSK9-related disorder
Short fetal femur length
Low density lipoprotein cholesterol level quantitative trait locus 1
Hypocholesterolemia
See cases
Lung cancer
Cervical cancer
Homozygous familial hypercholesterolemia
Key Variants
All Variants (167)
RSID Category Clinical Significance Conditions
RS746705490 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS747002272 Health Risk Conflicting classifications of pathogenicity Cardiovascular phenotype, Hypercholesterolemia, autosomal dominant
RS748933873 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS749049179 Health Risk Conflicting classifications of pathogenicity Cardiovascular phenotype, Hypercholesterolemia, autosomal dominant
RS749072203 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS749573024 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS750836360 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS751649334 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS751873016 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS753505066 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS753857795 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS754143671 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, familial, 1
RS755197912 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Cardiovascular phenotype, Hypercholesterolemia
RS7552471 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, familial, 1
RS755522807 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, familial, 1
RS755817854 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS757143429 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS757194881 Health Risk Conflicting classifications of pathogenicity Hypobetalipoproteinemia, Familial hypercholesterolemia, Hypercholesterolemia
RS758580558 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS758946245 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Cardiovascular phenotype, Hypercholesterolemia
RS760558712 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS760981278 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, familial, 1
RS761104090 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS763029049 Health Risk Conflicting classifications of pathogenicity Hypobetalipoproteinemia, Hypercholesterolemia, autosomal dominant
RS763855534 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Cardiovascular phenotype, Hypercholesterolemia
RS764603059 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS765583923 Health Risk Conflicting classifications of pathogenicity Hypobetalipoproteinemia, Hypercholesterolemia, autosomal dominant
RS767286042 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS769163891 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS770592607 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS771978846 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS772331713 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS772677312 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, familial, 1
RS774385716 Health Risk Conflicting classifications of pathogenicity Cardiovascular phenotype, Hypercholesterolemia, autosomal dominant
RS775521571 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS775988212 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Cardiovascular phenotype, Familial hypercholesterolemia
RS776367625 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS778562344 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS778738291 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS778849441 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS779384470 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Cardiovascular phenotype, Hypercholesterolemia
RS780193533 Health Risk Conflicting classifications of pathogenicity Cardiovascular phenotype, Hypercholesterolemia, autosomal dominant
RS780948835 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Cardiovascular phenotype, Hypercholesterolemia
RS793888521 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, familial, 1
RS886038746 Health Risk Conflicting classifications of pathogenicity Familial hypercholesterolemia, Hypercholesterolemia, autosomal dominant
RS886039837 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, familial, 1
RS886039839 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, familial, 1
RS886046433 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS886046436 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, autosomal dominant, 3
RS891322948 Health Risk Conflicting classifications of pathogenicity Hypercholesterolemia, familial, 1
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