COL4A1 Chromosome 13

Collagen type IV alpha 1 chain
400 variants 400 Health Risk

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What This Gene Does
This gene encodes a type IV collagen alpha protein. Type IV collagen proteins are integral components of basement membranes. This gene shares a bidirectional promoter with a paralogous gene on the opposite strand. The protein consists of an amino-terminal 7S domain, a triple-helix forming collagenous domain, and a carboxy-terminal non-collagenous domain. It functions as part of a heterotrimer and interacts with other extracellular matrix components such as perlecans, proteoglycans, and laminins. In addition, proteolytic cleavage of the non-collagenous carboxy-terminal domain results in a biologically active fragment known as arresten, which has anti-angiogenic and tumor suppressor properties. Mutations in this gene cause porencephaly, cerebrovascular disease, and renal and muscular defects. Alternative splicing results in multiple transcript variants. [provided by RefSeq, Dec 2014]
Gene Info
Gene Group
Network forming collagens
Locus Type
gene with protein product
Location
13q34
Ensembl
ENSG00000187498
Associated Conditions (44)
COL4A1-related disorder
Brain small vessel disease 1 with or without ocular anomalies
Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome
Microangiopathy and leukoencephalopathy
pontine
autosomal dominant
Retinal arterial tortuosity
Hemorrhage
intracerebral
susceptibility to
Inborn genetic diseases
Intellectual disability
Congenital anomaly of kidney and urinary tract
Schizencephaly
Uterine carcinosarcoma
Primary membranoproliferative glomerulonephritis
Optic nerve hypoplasia
Chronic kidney disease
Melanoma
HANAC-like syndrome
+24 more conditions
Key Variants
RS1004640402
Conflicting classifications of pathogenicity
COL4A1-related disorder, COL4A1-related disorder
Health Risk
RS1013805396
Conflicting classifications of pathogenicity
Health Risk
RS1057517719
Conflicting classifications of pathogenicity
Health Risk
RS1057519191
Conflicting classifications of pathogenicity
Health Risk
RS1064796811
Conflicting classifications of pathogenicity
Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
Health Risk
RS1085307967
Conflicting classifications of pathogenicity
Health Risk
RS113651836
Conflicting classifications of pathogenicity
Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome, Brain small vessel disease 1 with or without ocular anomalies, Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome
Health Risk
RS1179536054
Conflicting classifications of pathogenicity
Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome, Brain small vessel disease 1 with or without ocular anomalies, Microangiopathy and leukoencephalopathy
Health Risk
RS1348341976
Conflicting classifications of pathogenicity
Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
Health Risk
RS138266832
Conflicting classifications of pathogenicity
Inborn genetic diseases, Intellectual disability, Inborn genetic diseases
Health Risk
RS138269346
Conflicting classifications of pathogenicity
Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome, Inborn genetic diseases, Brain small vessel disease 1 with or without ocular anomalies
Health Risk
RS138503916
Conflicting classifications of pathogenicity
COL4A1-related disorder, Inborn genetic diseases, COL4A1-related disorder
Health Risk
All Variants (400)
RSID Category Clinical Significance Conditions
RS1555302922 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS1555302942 Health Risk Pathogenic Inborn genetic diseases, Inborn genetic diseases
RS1566353677 Health Risk Pathogenic
RS1566378788 Health Risk Pathogenic Abnormal cerebral morphology, Abnormal cerebral morphology
RS1594555106 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS1594566006 Health Risk Pathogenic
RS1594568948 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS1594579579 Health Risk Pathogenic Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome, Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome
RS1876438936 Health Risk Pathogenic Microangiopathy and leukoencephalopathy, pontine, autosomal dominant
RS1876543576 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, See cases, COL4A1-related disorder
RS1877783774 Health Risk Pathogenic Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome, Brain small vessel disease 1 with or without ocular anomalies, Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome
RS1877832657 Health Risk Pathogenic Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome, Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome
RS1877962670 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS1878012979 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS1878257364 Health Risk Pathogenic Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome, Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome
RS2138415342 Health Risk Pathogenic Microangiopathy and leukoencephalopathy, pontine, autosomal dominant
RS2139146124 Health Risk Pathogenic
RS2139149159 Health Risk Pathogenic
RS2139149224 Health Risk Pathogenic Cerebral palsy, Cerebral palsy
RS2139154554 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS2139156141 Health Risk Pathogenic
RS2139156207 Health Risk Pathogenic
RS2139159594 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS2139160399 Health Risk Pathogenic Porencephaly, Porencephaly
RS2139161185 Health Risk Pathogenic
RS2139162697 Health Risk Pathogenic
RS2139162781 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS2139163087 Health Risk Pathogenic
RS2139163985 Health Risk Pathogenic
RS2139165521 Health Risk Pathogenic
RS2139173063 Health Risk Pathogenic
RS2139173182 Health Risk Pathogenic
RS2139174027 Health Risk Pathogenic
RS2139204356 Health Risk Pathogenic
RS2139207389 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS2139245731 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS2495327532 Health Risk Pathogenic
RS2501580024 Health Risk Pathogenic
RS2501590728 Health Risk Pathogenic
RS2501590784 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
RS2501592907 Health Risk Pathogenic Microangiopathy and leukoencephalopathy, pontine, autosomal dominant
RS2501603480 Health Risk Pathogenic
RS2501749650 Health Risk Pathogenic Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome, Autosomal dominant familial hematuria-retinal arteriolar tortuosity-contractures syndrome
RS2501761275 Health Risk Pathogenic
RS2501761313 Health Risk Pathogenic
RS2501761416 Health Risk Pathogenic
RS2501770952 Health Risk Pathogenic
RS2501770978 Health Risk Pathogenic COL4A1-related disorder, COL4A1-related disorder
RS2501771259 Health Risk Pathogenic
RS2501773131 Health Risk Pathogenic Brain small vessel disease 1 with or without ocular anomalies, Brain small vessel disease 1 with or without ocular anomalies
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