ADSS1 Chromosome 14

Adenylosuccinate synthase 1
27 variants 27 Health Risk

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What This Gene Does
This gene encodes a member of the adenylosuccinate synthase family of proteins. The encoded muscle-specific enzyme plays a role in the purine nucleotide cycle by catalyzing the first step in the conversion of inosine monophosphate (IMP) to adenosine monophosphate (AMP). Mutations in this gene may cause adolescent onset distal myopathy. Alternative splicing results in multiple transcript variants. [provided by RefSeq, Feb 2016]
Associated Conditions (10)
Myopathy
distal
5
ADSS1-related disorder
Inborn genetic diseases
Ovarian serous cystadenocarcinoma
Acute myeloid leukemia
Colon adenocarcinoma
Arthrogryposis multiplex congenita
Fetal akinesia deformation sequence 1
Key Variants
All Variants (27)
RSID Category Clinical Significance Conditions
RS111588752 Health Risk Conflicting classifications of pathogenicity Myopathy, distal, 5
RS141465951 Health Risk Conflicting classifications of pathogenicity Myopathy, distal, 5
RS2541995490 Health Risk Conflicting classifications of pathogenicity
RS753588351 Health Risk Conflicting classifications of pathogenicity Myopathy, distal, 5
RS1890853802 Health Risk Likely pathogenic Myopathy, distal, 5
RS2140833479 Health Risk Likely pathogenic
RS376223981 Health Risk Likely pathogenic Ovarian serous cystadenocarcinoma, Acute myeloid leukemia, Ovarian serous cystadenocarcinoma
RS761489014 Health Risk Likely pathogenic Colon adenocarcinoma, Colon adenocarcinoma
RS767003671 Health Risk Likely pathogenic
RS774425831 Health Risk Likely pathogenic Myopathy, distal, 5
RS946575582 Health Risk Likely pathogenic
RS1175622794 Health Risk Pathogenic Myopathy, distal, 5
RS1358620767 Health Risk Pathogenic
RS1415601575 Health Risk Pathogenic
RS1891337397 Health Risk Pathogenic
RS1891497352 Health Risk Pathogenic Myopathy, distal, 5
RS2140828534 Health Risk Pathogenic
RS2542040039 Health Risk Pathogenic
RS2542049491 Health Risk Pathogenic
RS559454746 Health Risk Pathogenic Myopathy, distal, 5
RS760706338 Health Risk Pathogenic
RS769542442 Health Risk Pathogenic Arthrogryposis multiplex congenita, Fetal akinesia deformation sequence 1, Myopathy
RS777908589 Health Risk Pathogenic
RS781756056 Health Risk Pathogenic
RS140614802 Health Risk Pathogenic/Likely pathogenic Myopathy, distal, 5
RS1566800987 Health Risk Pathogenic/Likely pathogenic Myopathy, distal, 5
RS756832498 Health Risk Pathogenic/Likely pathogenic Myopathy, distal, 5
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